Spark Therapeutics

Spark Therapeutics Focuses on the Development of Gene Therapies, Aiming to Extend the Lives and Improve the Quality of Life for Patients with Debilitating Genetic Diseases through One-Time, Life-Altering Treatments. Spark Therapeutics has Established a Leading Integrated Gene Therapy Platform, and We are Committed to Transforming Genes into Medicines for Patients with Genetic Disorders, Including Inherited Retinal Diseases (IRDs), Liver Diseases such as Hemophilia, Lysosomal Storage Disorders like Pompe and Fabry, as well as Neurodegenerative Diseases.