Orchard Therapeutics

Orchard Therapeutics is a biotechnology company registered in September 2015, dedicated to providing revolutionary and innovative gene therapies for patients with severe, life-threatening orphan diseases (rare diseases). Within the company’s gene therapy development programs, it aims to develop innovative ex vivo autologous hematopoietic stem cell gene therapies. By leveraging the therapeutic potential of these groundbreaking gene therapies, the company seeks to restore the defective gene functions associated with severe, life-threatening hereditary disorders.